Collaboration

Currently running collaborative projectsin CCP

  • Preclinical safety study for Ctnnb1 foundation (Slovenia)
  • Proof of concept study for Bow foundation (USA)
  • Proof of concept study for Genteo (CZ)
  • Proof of concept study, & preclinical testing for Asgent (CZ)

IMTM: First RD in the program

  • Diamond-Blackfan anemia and other ribosomopathies
  • Cystic fibrosis
  • Hereditary and rare cancers

Preclinical and clinical diagnostic sand therapeutics development at the IMTM

  • To provide access to high-end research infrastructure, including genome sequencing, protemics, metabolomics, biobanking, bioinformatics, high-throughput screening technologies, animal imaging and animal models core facilities.
  • To provide clinical and preclinical regulatory expertise in development of diagnostics and therapeutics.
  • To perform specialized certified services required for the regulatory process (under ISO 17025, ISO 15189, good laboratory practice), etc.

Currently running collaborative projects at IMTM/EATRIS-CZ

  • CFTR (Cystic fibrosis transmembrane conductance regulator) modulators – development of cellular models of relevant disease mutations with unmet need, screening candidates for CFTR correctors/modulators.
  • Clinical development of fenretinide for cystic fibrosis patients (LaurentPharma)

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